Urgent action needed to make Spinraza available – Clinicians/SMA charities call for progress

Yesterday, clinicians and SMA charities expressed the urgent need for action to progress Spinraza being made available to all who may benefit. Grave concerns were raised highlighting the lengthy process for NHS England and NICE appraisal of nusinersen; the lack of clarity of the appropriate choice of process for NICE to use for appraisal; the implications of these choices for the well-being and clinical outcomes of individuals living with SMA.

Read the letter sent to NICE, NHS England and the National Institute for Health Research here.

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